Research

One Step Closer to LAMA2-RD Clinical Trials: Modalis Therapeutics

Gustavo Dziewczapolski, Scientific Director

Sep 302 min read

One Step Closer to LAMA2-RD Clinical Trials: Modalis Therapeutics

Modalis Therapeutics program for LAMA2-RD gene therapy granted Rare Pediatric Disease Designation by FDA.

Gustavo Dziewczapolski, Scientific Director

Sep 235 min read

Research Update: LMNA

We are honored to support groundbreaking discoveries related to LMNA-CMD.

Workshop to Establish Subtype-Specific Care Recommendations for Congenital Muscular Dystrophy

Cure CMD

Sep 12 min read

Workshop to Establish Subtype-Specific Care Recommendations for Congenital Muscular Dystrophy

We are thrilled to announce a new clinical workshop focused on establishing CMD subtype-specific care recommendations.

Gustavo Dziewczapolski, Scientific Director

Aug 73 min read

Research Update: Dystroglycanopathy

We are honored to support groundbreaking discoveries related to Dystroglycanopathy.

Gustavo Dziewczapolski, Scientific Director

Jul 24 min read

Research Update: LAMA2

We are honored to support groundbreaking discoveries related to LAMA2-Related Dystrophy.

iMM Joins the MAGIC Consortium to Advance Research on Muscular Dystrophies

Gustavo Dziewczapolski, Scientific Director

Jun 62 min read

iMM Joins the MAGIC Consortium to Advance Research on Muscular Dystrophies

The MAGIC research team welcomes iMM to the consortium to add a cellular perspective to muscle-on-chip technologies

Rachel Alvarez

Jun 52 min read

Omigapil Publication Now Available

Long-awaited publication about the Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy now published.

Gustavo Dziewczapolski, Scientific Director

May 284 min read

Research Update: SELENON

We are honored to support groundbreaking discoveries related to SELENON-Related Disorders.

Interview with Gustavo Dziewczapolski: Doctor in Neuropharmacology and Scientific Director of Cure CMD

Giulia Da Re

May 2318 min read

Interview with Gustavo Dziewczapolski: Doctor in Neuropharmacology and Scientific Director of Cure CMD

Explore an in-depth interview with Gustavo Dziewczapolski, Doctor in Neuropharmacology and Scientific Director of Cure CMD. Gain insights in

Gustavo Dziewczapolski, Scientific Director

May 12 min read

2024 Myology Congress Recap

Cure CMD’s Scientific Director, Dr. Gustavo Dziewczapolski, provides a recap of his attendance at the 8th International Myology Congress in

Gustavo Dziewczapolski, Scientific Director

Apr 164 min read

Research Update: Collagen 6

We are honored to support groundbreaking discoveries in Collagen 6-Related Dystrophies (COL6-RD).

Cure CMD

Sep 29, 20232 min read

An Exciting Milestone for LAMA2-CMD

Expanding on nearly a decade of partnership in the life sciences, the Translational Sciences team at UPMC Enterprises and the University...

Cure CMD

Jul 31, 20231 min read

Team Cure CMD Raises $140K to Support CMD Research

This year, the MDBR's Team Cure CMD raised $140k for research.

A Profound Void in our Hearts: The Loss of Prof. Jeanette Erdmann

Cure CMD

Jul 11, 20232 min read

A Profound Void in our Hearts: The Loss of Prof. Jeanette Erdmann

Prof. Jeanette Erdmann, CMD Researcher and CMD-affected individual passed away unexpectedly after a tragic fall.

Cure CMD

Nov 21, 20223 min read

Cure CMD Announces 2022 Research Grants

$482,000 Awarded for CMD Science We are thrilled to announce the newest round of research grants focused on congenital muscular...

$3 Million to Provide Foundational Knowledge: The Pediatric Cell Atlas of Skeletal Muscle

Terry Selucky

Apr 4, 20224 min read

$3 Million to Provide Foundational Knowledge: The Pediatric Cell Atlas of Skeletal Muscle

On the road toward treatments and a cure for congenital muscular dystrophy, we’ve come a long, long way to learn about causes and...

2021 SciFam Content Now Available on YouTube

Rachel Alvarez

Sep 3, 20211 min read

2021 SciFam Content Now Available on YouTube

Thanks to everyone who participated in our 2021 Virtual SciFam Conference. If you didn't get a chance to attend or watch recordings in...

Terry Selucky

Aug 30, 20212 min read

Congratulations Dr. Erdmann!

Congratulations CMD Researcher and Community Member, Dr. Jeannette Erdmann! We are thrilled to share that CMD researcher and...

Cure CMD

Apr 30, 20212 min read

SciFam 2021 is Around the Corner

An all-virtual conference will cover care and research, and events for kiddos! It’s been way too long since July 2019, when many of us...

Meet Jaclyn: Scientist, Affected Individual and Advocate

Terry Selucky

Feb 3, 20215 min read

Meet Jaclyn: Scientist, Affected Individual and Advocate

Jaclyn Prystupa was always interested in science. In school, biology was her favorite subject, and the Saskatchewan Science Centre was...