Gustavo Dziewczapolski, Scientific DirectorSep 302 min readOne Step Closer to LAMA2-RD Clinical Trials: Modalis TherapeuticsModalis Therapeutics program for LAMA2-RD gene therapy granted Rare Pediatric Disease Designation by FDA.
Rachel AlvarezJun 52 min readOmigapil Publication Now AvailableLong-awaited publication about the Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy now published.
Cure CMDApr 4, 201811 min readSanthera Announces Successful Completion of First Clinical Trial with Omigapil in Patients with CongPlease see the end of this article for Frequently Asked Questions - CALLISTO Phase 1 Clinical Trial Pratteln, Switzerland, April 5, 2018...