The FDA’s first Platform Technology Designation marks a major step forward for rare disease treatments, allowing reuse of key therapy components across related conditions. This breakthrough could accelerate CMD therapies, but Cure CMD needs your support to keep the momentum going.

Learn how Cure CMD is fighting harmful legislation like the OBBBA, NIH funding cuts, and threats to Medicaid through strategic advocacy and rare disease policy action. Discover how you can help protect access to care, advance research, and make your voice heard.

This Father’s Day, Cure CMD celebrates the strength, insight, and quiet resilience of dads raising children with congenital muscular dystrophy. In this special blog a group of CMD dads reflect on what they’ve learned, how they stay grounded, and the unique connections they share with their children.

From shaping care guidelines in the Netherlands to tackling gene therapy challenges at the MDA Summit, Cure CMD is driving progress in research and care. Join us at the 2025 SciFam Conference this August in Philadelphia—registration is open!

In honor of Mother’s Day 2025, Cure CMD asked five incredible mothers to reflect on caregiving, resilience, and the unexpected joys of...

CMD Community Member, Ashley Burkman, has written a new book, “Move,” featuring characters living with congenital muscular dystrophy.

Cure CMD’s Community Engagement Manager and tireless advocate for the rare disease and disability communities, was recently featured by her Alma mater's campus magazine, the University of Kentucky’s UKNow.

Q&A: Cure CMD’s Executive Director, Rachel Alvarez, gives in-depth insight into what to expect at the 2025 SciFam Conference.

Click the button at the bottom of the page to mail your representative now! On April 1, the U.S. Department of Health and Human Services...

CMD Advocates gathered in Washington, DC to honor, celebrate & champion for those living with rare disease.

CMD Community Member, Justin Moy, shares his journey with LAMA2-related muscular dystrophy and his life quest to cure his own condition.

The Cure CMD Legislative Advocacy team, along with our advocacy partners, continue to actively monitor developments and will provide updates