Category Archives: News from Other Sources

News gathered from external sources by our RSS aggregator.

Discovery of navigation system used by cancer, nerve cells

Duke University researchers have found a “roving detection system” on the surface of cells that may point to new ways of treating diseases like cancer, Parkinson’s disease and amyotrophic lateral…

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What is ALS? What causes ALS?

Amyotrophic lateral sclerosis (ALS) is a fatal degenerative neurological condition, also referred to as Lou Gehrig’s disease. It weakens the muscles and impacts body functioning.

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Gene therapy protects mice from Duchenne muscular dystrophy-related heart condition

A new gene therapy developed by researchers at the University of Missouri School of Medicine has shown to protect mice from a life-threatening heart condition caused by muscular dystrophy.

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Missing protein restored in patients with muscular dystrophy

Advances in the treatment of muscular dystrophy: For the first time, a research team has succeeded in restoring a missing repair protein in skeletal muscle of patients with muscular dystrophy.

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Researchers find RNA-targeted drug candidate for Lou Gehrig’s disease

By targeting RNA molecules that tangle and clump in the nervous systems of patients with the most common genetic form of amyotrophic lateral sclerosis (ALS or Lou Gehrig’s disease) and frontotemporal…

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New small molecules target mutation in ALS and a form of dementia

Researchers have targeted a specific genetic mutation that causes ALS and FTD, and the small-molecule drug candidates they created could help treat patients with these diseases.

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New form of dystrophin protein discovered; could lead to therapy for some Duchenne muscular dystrophy patients

Scientists have discovered a new form of dystrophin, a protein critical to normal muscle function, and identified the genetic mechanism responsible for its production.

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Potential ALS treatment avenue identified

A series of studies begun by Harvard Stem Cell Institute (HSCI) scientists eight years ago has lead to a report just published that may be a major step forward in the quest to develop real treatments…

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New mechanism found for neurodegeneration

A research team led by Jackson Laboratory Professor and Howard Hughes Investigator Susan Ackerman, Ph.D.

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‘Pathogenic connection’ between cancer and autoimmune disorders

Researchers developing a potential vaccine for myasthenia gravis find that an inhibitor expressed in tumors is also found in people who have this disease.

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  • Congenital Muscular Dystrophy

    A group of diseases causing muscle weakness at birth. Several defined genetic mutations cause muscles to break down faster than they can repair or grow. A child with CMD may have various neurological or physical impairments. Some children never gain the ability to walk, while others lose the ability as they grow older. Learn more...

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