Category Archives: News from Other Sources

An 11½-minute interview with researcher Stephen Tapscott explores recent findings about the molecular basis of facioscapulohumeral MD

The Muscular Dystrophy Association’s latest round of grants allocates more than $12 million to the support of 38 research projects investigating the causes of, and potential treatments for, a number of forms of neuromuscular disease.

Jacobus is inviting 30 selected individuals with Lambert-Eaton myasthenic syndrome to participate in a placebo-controlled trial of 3,4-DAP.

The grants fund six new ALS projects, each using a different mechanism to uncover the causes of the disease and potential treatments.

MDA has awarded 38 grants totaling more than $12 million to support research into general muscle health and more than 15 neuromuscular diseases in its program.

Pharmaceuticals will test its experimental antisense drug in 24 children with spinal muscular atrophy at five U.S. centers.

NurOwn stem cell technology, currently being tested in Israel, appears safe and seems to improve breathing, swallowing and muscle strength.

Molecular geneticist Stephen Wilton discusses his group’s development of exon-skipping compounds to restore dystrophin production in Duchenne MD.

Four children not making any acid maltase enzyme tolerated enzyme replacement therapy when also treated with immunosuppressants.

MDA’s $1 million grant will help fund the development of TVN-102, which attracts the muscle protein utrophin to the muscle-fiber membrane.