Duke University researchers have found a “roving detection system” on the surface of cells that may point to new ways of treating diseases like cancer, Parkinson’s disease and amyotrophic lateral…
Amyotrophic lateral sclerosis (ALS) is a fatal degenerative neurological condition, also referred to as Lou Gehrig’s disease. It weakens the muscles and impacts body functioning.
A new gene therapy developed by researchers at the University of Missouri School of Medicine has shown to protect mice from a life-threatening heart condition caused by muscular dystrophy.
Advances in the treatment of muscular dystrophy: For the first time, a research team has succeeded in restoring a missing repair protein in skeletal muscle of patients with muscular dystrophy.
By targeting RNA molecules that tangle and clump in the nervous systems of patients with the most common genetic form of amyotrophic lateral sclerosis (ALS or Lou Gehrig’s disease) and frontotemporal…
Researchers have targeted a specific genetic mutation that causes ALS and FTD, and the small-molecule drug candidates they created could help treat patients with these diseases.
Scientists have discovered a new form of dystrophin, a protein critical to normal muscle function, and identified the genetic mechanism responsible for its production.
A series of studies begun by Harvard Stem Cell Institute (HSCI) scientists eight years ago has lead to a report just published that may be a major step forward in the quest to develop real treatments…
A research team led by Jackson Laboratory Professor and Howard Hughes Investigator Susan Ackerman, Ph.D.
Researchers developing a potential vaccine for myasthenia gravis find that an inhibitor expressed in tumors is also found in people who have this disease.