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Congenital Muscular Dystrophy
A group of diseases causing muscle weakness at birth. Several defined genetic mutations cause muscles to break down faster than they can repair or grow. A child with CMD may have various neurological or physical impairments. Some children never gain the ability to walk, while others lose the ability as they grow older. Learn more...-
Upcoming Fundraisers
- Minnesota 1/2 Marathon
4 August 2011
St Paul, MN - Ruby's Diner Hosts Cure CMD Fundraiser
19 February 2012
Rolling Hills Estates, CA 90274 - Long Branch 1/2 Marathon
6 May 2012
Long Branch, NJ - Charlie's Take Me Out To The Ballgame!!
8 July 2012
New York - Disneyland 1/2 Marathon
2 September 2012
Anaheim, CA
- Minnesota 1/2 Marathon
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PTC Therapeutics Completes Enrollment Of Pivotal Trial In Muscular Dystrophy
PTC Therapeutics, Inc. (PTC) announced that it has successfully completed patient enrollment of its pivotal clinical trial of PTC124 in patients with nonsense mutation Duchenne and Becker muscular dystrophy (nmDMD/BMD). Accrual was completed two months ahead of schedule. The company also announced today that PTC124 has been issued the generic name, ataluren.
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